CHAMGAP
APPROVEDReviewed and approved by the Chamgap Editorial Team (2026-07-18). The draft was written by AI, the existence of all 5 cited sources was verified at the original page, and the verdict passed blind grading and adversarial audit. Methodology v0.6.
Verdict No. 487 · Search date 2026-07-18 · Methodology v0.6

Tauroursodeoxycholic acid,
does it really help with Slowing ALS progression and extending survival?

30-Second Summary
D
Evidence Grade D · 28 · Safety caution
Unlike the early signal, the large phase 3 trial did not improve ALS function or survival
What the
research shows
An early 34-person phase 2 trial suggested slower functional decline when TUDCA 2 g/day was added to riluzole, but the confirmatory 18-month TUDCA-ALS phase 3 trial in 336 participants across 25 centers in seven countries was null for the primary ALS Functional Rating Scale-Revised endpoint, survival, and neurofilament light. This decisive null result from one confirmatory phase 3 trial supports D, not F, which would require repeated confirmatory contradiction.
What the
ads claim
Marketing and patient discussions turn preclinical phrases such as bile-acid neuroprotection, mitochondrial protection, and reduced motor-neuron death into claims of slower ALS progression. Mechanistic plausibility is not the same as improved function or survival in humans, and the confirmatory trial did not support the latter.
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Useful facts when choosing a product

  • Consumers in Korea can encounter imported TUDCA supplements such as 250-mg capsules, but these are not equivalent to an approved ALS medicine.
  • The phase 2 and phase 3 trials added TUDCA 1 g twice daily, or 2 g/day, to riluzole and other standard care. This equals eight 250-mg capsules daily.
  • Purity, content, enteric properties, and impurity control of supplements cannot be assumed to match the investigational medicinal product.
  • The phase 3 product was generally well tolerated, with mostly mild gastrointestinal effects, but long-term high-dose self-treatment, hepatobiliary disease, and concomitant medicines warrant specialist review. It must not replace standard ALS care.
Gap Measurement · Verdict 487 · D 28
What advertising claims
What independent, higher-quality research supports
△ GAP
01

What the research actually shows

The 2016 Elia proof-of-principle trial assigned 34 patients with ALS receiving riluzole to TUDCA 1 g twice daily or placebo for 54 weeks and reported responder and functional-decline signals. TUDCA-ALS tested this finding in a randomized double-blind phase 3 trial at 25 centers in seven countries; 336 of the planned 440 participants enrolled. At 18 months, the ALS Functional Rating Scale-Revised responder endpoint, survival time, and neurofilament light were all nonsignificant. PHOENIX studied AMX0035, a sodium phenylbutyrate-taurursodiol combination, in 664 participants and was not a confirmatory trial of TUDCA alone.

02

Why this is classified as D (28)

A small randomized phase 2 signal exists, but the larger 336-person, 18-month multinational phase 3 trial was null for the primary functional endpoint, survival, and biomarkers. One decisive null confirmatory trial supports D with 28 points. PHOENIX cannot establish repeated contradiction because it tested a combination product rather than TUDCA alone.

Counterpoint. Recruitment shortfall and attrition during the coronavirus pandemic leave room for exploratory analyses by progression speed. Post hoc subgroup hypotheses do not reverse the overall phase 3 failure.

Rejudgment record. Reassessment (cross-check reflected) — Prioritized the null functional, survival, and biomarker results from the 336-person, 18-month multinational confirmatory phase 3 trial over the 34-person phase 2 signal, while excluding the AMX0035 PHOENIX combination trial from repeated contradiction of TUDCA alone

Sub-claim grades by effect

This ingredient is marketed for several effects. A single overall grade blends strong and weak claims together, so each effect is graded separately here. The overall grade reflects the strongest disconfirming or core claim.

Effect (sub-claim)GradeBasis
Slowing functional decline and disease progression in ALSDThe primary responder endpoint based on the ALS Functional Rating Scale-Revised was null in the single 336-person, 18-month confirmatory phase 3 trial
Extending survival in ALSDSurvival time did not differ significantly in the same single confirmatory phase 3 trial

Cross-check — Codex and Claude

This verdict was drafted by Codex through literature review and source-existence checks, cross-checked through blind grading and adversarial audit, and settled by reapplying the methodology boundary rules. Cases with split grades were resolved through rejudgment.
03

Evidence Table

StudyDesignSampleFundingEndpointResultWeight
Elia AE et al. 2016Randomized double-blind placebo-controlled phase 2 proof-of-principle trial34Investigator-led, noncommercial supportALS Functional Rating Scale-Revised responders, functional decline, and safetyAn early signal of slower functional decline was reported with add-on TUDCA 1 g twice daily.Early positive
TUDCA-ALS Consortium 2024Randomized double-blind placebo-controlled multinational phase 3 trial18European public and research-consortium support with study product suppliedALS Functional Rating Scale-Revised responders, survival time, and neurofilament lightThe primary endpoint failed, with no significant difference in survival time or the biomarker.Decisive contradiction
Lombardo F et al. 2023Phase 3 statistical analysis plan336TUDCA-ALS consortiumPrespecified responder analysis based on the ALS Functional Rating Scale-Revised and secondary outcomesThe analysis and endpoints were documented before results were announced.Methodological
Paganoni S et al. 2020; PHOENIX 2024Phase 2 and subsequent phase 3 trials of AMX0035664Amylyx PharmaceuticalsALS Functional Rating Scale-Revised, survival, and prespecified primary and secondary outcomesAfter an early combination-product signal, PHOENIX failed its prespecified endpoints and the product was withdrawn.Combination-product context
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Receipt — 5 References

All 5 cited sources were verified for existence at the original page (as of 2026-07-18).

Elia AE, Lalli S, Monsurro MR, et al. Tauroursodeoxycholic acid in the treatment of patients with amyotrophic lateral sclerosis. Eur J Neurol. 2016;23(1):45-52. PMID: 25664595. DOI: 10.1111/ene.12664.
checked
Lombardo F, Albanese A, Bruschettini M, et al. A randomized double-blind clinical trial on safety and efficacy of tauroursodeoxycholic acid as add-on treatment in patients affected by amyotrophic lateral sclerosis: the statistical analysis plan of TUDCA-ALS trial. Trials. 2023;24:792. PMID: 38053196. DOI: 10.1186/s13063-023-07638-w.
checked
TUDCA-ALS Consortium. Announcement of top-line results from the TUDCA-ALS phase 3 trial. March 27, 2024. ClinicalTrials.gov NCT03800524.
checked
Paganoni S, Macklin EA, Hendrix S, et al. Trial of Sodium Phenylbutyrate-Taurursodiol for Amyotrophic Lateral Sclerosis. N Engl J Med. 2020;383(10):919-930. PMID: 32877582. DOI: 10.1056/NEJMoa1916945.
checked
Amylyx Pharmaceuticals, Inc. Form 10-Q for the quarter ended March 31, 2024. Filed May 10, 2024. PHOENIX trial and RELYVRIO/ALBRIOZA discontinuation statement.
checked
Draft and rewrite: Codex (AI) · Verification: Codex blind grading and adversarial audit · Final adjudication: Claude
Reviewed and approved: Chamgap Editorial Team · Approval date: 2026-07-18 · Corrections: none

Cite this verdict

Tauroursodeoxycholic acid (TUDCA) x slowing ALS progression and extending survival Evidence Grade D card
[Chamgap] Tauroursodeoxycholic acid (TUDCA) x slowing ALS progression and extending survival — Evidence Grade D·28. 5 cited sources checked. Source: https://chamgap.com/en/verdicts/general/tudca-als-progression-survival/ · CC BY 4.0

CC BY 4.0 — free to use with attribution; do not distort grades, numbers, or verdict meaning.

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What this document does and does not do

Chamgap is an information source. It reports what research has and has not confirmed; it does not tell readers what to take or buy. That decision belongs to readers and, when needed, medical or legal professionals. This verdict reflects literature available up to the search date and may change as new research appears. Nothing here is medical advice.